Search for Clinical Trial Results
Lysosomal Storage Diseases, Nervous System - 25 Studies Found
Status | Study |
Recruiting |
Study Name: Long-term Outcome in Late-onset Pompe Disease Treated Beyond 36 Months (ATBIG-Pompe-Study) Condition: Pompe Disease Date: 2016-06-20 Interventions: Drug: glucosidase alfa Long-term use in an observational study of licenced drug |
Recruiting |
Study Name: Respiratory Muscle Training in L-Onset Pompe Disease (LOPD) Condition: Glycogen Storage Disease Type II Date: 2016-06-13 Interventions:
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Recruiting |
Study Name: Study to Compare the Efficacy and Safety of Enzyme Replacement Therapies neoGAA and Alglucosidase Alfa Administered Every Other Week in Patients With Late-onset Pompe Disease Who Have Not Been Previously Treated for Pompe Disease Condition: Glycogen Storage Disease Type II-Pompe's Disease Date: 2016-05-23 Interventions:
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Recruiting |
Study Name: Identification of Tongue Involvement in Late-Onset Pompe Disease Condition:
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Recruiting |
Study Name: Pompe Disease QMUS and EIM Condition: Pompe Disease Date: 2016-04-11 Interventions:
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Enrolling by invitation |
Study Name: An MRI Study on Muscular Diseases -Pompe Disease and Dystrophia Myotonica- Condition:
Date: 2015-12-08 |
Active, not recruiting |
Study Name: First-In-Human Study to Evaluate Safety, Tolerability, and PK of Intravenous ATB200 Alone and When Co-Administered With Oral AT2221 Condition: Pompe Disease Date: 2016-01-26 Interventions:
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Recruiting |
Study Name: Safety and Effectiveness of Resistance Exercise Training in Patients With Pompe Disease. Condition:
Date: 2015-12-10 Interventions: Other: Resistance Exercise Training Resistance Exercise Tr |
Not yet recruiting |
Study Name: Prevalence of Pompe's Disease in Respiratory Clinics Condition: Pompe's Disease Date: 2015-08-17 Interventions: Other: Prospective observational study Prospective observational study collecting data during a clinic v |
Recruiting |
Study Name: Immune Modulation Therapy for Pompe Disease Condition: Pompe Disease Date: 2015-08-10 Interventions:
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